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Etuvetidigene Autotemcel 治疗 Wiskott–Aldrich 综合征
Etuvetidigene Autotemcel for the Treatment of Wiskott–Aldrich Syndrome
导读
该研究发表于 NEJM,评估了 Etuvetidigene Autotemcel 基因疗法治疗 Wiskott–Aldrich 综合征的效果。
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来源:NEJM · nejm.org